Muscular Dystrophy: Patient-reported outcomes
Patient-reported outcomes after stem cell therapy for Muscular Dystrophy, based on 51 patients in our follow-up registry.
Updated ·
Overall patient-reported outcomes
Physical condition
reported physical improvement
84%
N = 50
Quality of life
reported quality-of-life improvement
85%
N = 48
Treatment satisfaction
satisfied with the treatment outcome
78%
N = 50
Reported change vs. before treatment
Worse No change Small Moderate Significant
| Symptom | Reported change vs. before treatment | Reported improvement |
|---|---|---|
| Body pain | | 87% |
| Muscle stiffness | | 83% |
| Heart palpitations or arrhythmias | | 79% |
| Muscle cramps | | 77% |
| Enlarged muscles | | 74% |
| Difficulty swallowing | | 73% |
| Falls | | 72% |
| Loss of muscle mass | | 71% |
| Development delay (children) | | 71% |
| Walking | | 70% |
| Slurred speech | | 67% |
| Standing up | | 64% |
| Excessive sleeping or sleepiness | | 58% |
| Behaviour problems (children) | | 53% |
| Cognitive impairment | | 46% |
| Walking up stairs | | 43% |
| Droopy eye lids | | 40% |
About this data
Patients self-assess each symptom on a 5-point scale (Worse / No improvement / Small / Moderate / Significant) at follow-up checkpoints after treatment, comparing to their pre-treatment baseline. "Reported improvement" combines the small, moderate and significant buckets. Data is updated daily from our internal patient registry. As with any medical treatment, past results do not guarantee future outcomes — improvements vary from patient to patient.
