Nirma - SMA III Stem Cell Patient
Nirma traveled from Indonesia to China to receive transplants of umbilical cord blood stem cells--a form of adult stem cells--to treat symptoms associated with Spinal Muscular Atrophy Type III. SMA III is caused by a rare genetic mutation. While the treatment she received is not a cure for SMA III it can offer progressive quality of life improvements for a patient.
Improvement statistics
Based on follow-up reports from 18 patients across 63 forms, here is the percentage who self-reported any improvement after treatment.
About this data
Patients self-assess each symptom on a 5-point scale (Worse / No improvement / Small / Moderate / Significant) at follow-up checkpoints after treatment, comparing to their pre-treatment baseline. "Reported improvement" combines the small, moderate and significant buckets. Data is updated daily from our internal patient registry. As with any medical treatment, past results do not guarantee future outcomes — improvements vary from patient to patient.
